Charity Partner Spotlight...

The AADC Research Trust

We’re proud to shine a light on The AADC Research Trust — a pioneering global charity founded in 2006 by families, for families impacted by Aromatic L-Amino Acid Decarboxylase Deficiency (AADC-D), one of the world’s rarest and most complex neurotransmitter disorders.

For nearly 20 years, the Trust has been a source of hope, guidance, and strength for families in over 30 countries — championing research, accelerating diagnosis, and providing life-changing resources to support those navigating this ultra-rare condition.



The Trust has been instrumental in advancing the field of gene therapy, supporting early access programmes and international clinical trials that helped pave the way for the first approved gene therapy for AADCd in both Europe and the United States.

Through tireless advocacy and collaboration, the AADC Research Trust continues to unite caregivers, clinicians, and scientists, fostering a global community committed to improving outcomes and raising awareness of this life-limiting disorder.

At INDConf LONDON 2025, we’re proud to stand alongside the Trust and celebrate their legacy of leadership, compassion, and unwavering dedication to change.

Hrabrisa (Lil Brave One)

We are proud to partner with Hrabriša – lil’ brave one, a Serbia-based non-profit organisation dedicated to supporting children affected by rare congenital neurotransmitter disorders, including AADC deficiency.

Founded by parents, Hrabriša leads with empathy and impact — building awareness, translating resources, and advocating for timely diagnosis and treatment in non-English-speaking communities. Through their commitment, they’ve helped families access life-changing care and global expertise.

In 2024, Hrabriša was awarded a prestigious grant from the Chan Zuckerberg Initiative’s Rare As One Network, recognising their leadership in the rare disease space and supporting their mission to amplify underrepresented patient voices on a global scale.

Their tireless efforts embody the heart of INDConf LONDON 2025: collaboration, inclusion, and community-powered progress.



SSADH Association

We are proud to welcome The SSADH Association as a charity partner for INDConf LONDON 2025.

Founded by parents and driven by a global community, the SSADH Association supports individuals affected by Succinic Semialdehyde Dehydrogenase (SSADH) Deficiency, an ultra-rare neurotransmitter disorder with complex neurological, metabolic, and developmental impacts.

From funding cutting-edge research initiatives and natural history studies to connecting families with specialists and resources worldwide, the association plays a vital role in bridging science and support. Their commitment to accelerating diagnosis, treatment, and therapeutic discovery continues to inspire progress across the rare disease field.

Their voice is instrumental in ensuring that SSADH is seen, heard, and understood — and we are honoured to stand alongside them at INDConf as we work to elevate collaboration across the entire neurotransmitter disorder community.

De Neu

We are proud to partner with De Neu, a Spain-based association dedicated to supporting families and advancing understanding of rare neurotransmitter disorders.

Founded as a meeting point for patients, caregivers, clinicians, and researchers, De Neu works tirelessly to:

• Promote and support scientific research aimed at improving quality of life for children with neurotransmitter disorders

• Raise awareness among healthcare professionals, educators, and the wider community

• Build strong networks of international cooperation to unite families and experts across borders

Through advocacy, education, and community-building, De Neu embodies the collaborative spirit at the heart of INDConf LONDON 2025 — ensuring that families are supported, research is prioritised, and progress is shared worldwide.